Washington, D.C., May 29, 2025 — _The Alliance for mRNA Medicines released the following statement in response to recent comments made by the US Department of Health and Human Services regarding mRNA technology:
mRNA is a revolutionary technology with therapeutic applications in serious and complex diseases, with high potential to save lives and improve the health of millions of Americans. It is already being tested in the clinic for patients with diseases that present with significant challenges to living a healthy and enriching life. These are American patients who have no effective treatment options – _diseases as diverse as pancreatic cancer and melanoma, cystic fibrosis, and cardiovascular, autoimmune, and neurological conditions. mRNA technology is also a critical—and proven—component of America’s leadership position in biotechnology and pharmaceutical industries, in academic leadership, and as a key factor in our national security strategy.
Advancements in mRNA technology are improving American lives today, demonstrated by the recent announcement of the successful treatment of an infant, Baby KJ. Baby KJ successfully received a personalized (N of 1) mRNA-CRISPR gene therapy treatment for severe carbamoyl phosphate synthetase 1 (CPS1) deficiency, which (until now) was an incurable, rare disease. This most recent story shows the potential of mRNA technologies. There are many other stories like this in the making. With strategic investments in the technology made through strong government partnership over the past decades and into the future, thousands and potentially millions of stories like this will become reality. Remaining committed to the American people through government and private investment in mRNA product development has the potential to save the lives of children from infancy to adolescents and meaningfully improve the lives of adults.
The US has a choice – to maintain our leadership position or to fall behind. Efforts to undermine mRNA investment and development jeopardize American health, threaten jobs and national security, and erode the success ignited by President Trump’s leadership during his first term.
About the Alliance for mRNA Medicines (AMM)
The Alliance for mRNA Medicines (AMM) is the leading global organization dedicated to advancing and advocating for mRNA and next-generation encoding RNA therapeutics and vaccines for the benefit of patients, public health, and society. Our mission is to propel the future of mRNA medicine, improve patients’ lives, and advance scientific knowledge by convening and empowering mRNA industry leaders, innovators, scientists, and other key stakeholders. Learn more at https://mrnamedicines.org
Media Contact:
Clay Alspach
Executive Director
Alliance for mRNA Medicines
[email protected]